News & Publications

A new class of therapies based on transfer RNA could treat forms of cystic fibrosis, muscular dystrophy, genetic epilepsies, and more

News

Publications

FEB 10, 2021

Therapeutic promise of engineered nonsense suppressor tRNAs

Nonsense mutations change an amino acid codon to a premature termination codon (PTC) generally through a single-nucleotide substitution…

FEB 18, 2019

Engineered transfer RNAs for suppression of premature termination codons

The appearance of the premature translation termination codons (PTCs)…